Drug Type AAV based gene therapy |
Synonyms MYO 301, MYO301, SRP-9006 |
Target |
Mechanism ANO5 stimulants(anoctamin 5 stimulants) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization Myonexus Therapeutics, Inc.Startup |
Inactive Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Muscular Dystrophies, Limb-Girdle | Preclinical | US | Myonexus Therapeutics, Inc.Startup | 03 May 2018 |