Drug Type AAV based gene therapy |
Synonyms MYO 301, MYO301, SRP-9006 |
Target |
Action stimulants |
Mechanism ANO5 stimulants(anoctamin 5 stimulants) |
Therapeutic Areas |
Active Indication- |
Inactive Indication |
Originator Organization |
Active Organization- |
Inactive Organization |
Drug Highest PhasePendingPreclinical |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Muscular Dystrophies, Limb-Girdle | Preclinical | United States | 03 May 2018 |