Drug Type AAV based gene therapy |
Synonyms |
Target |
Action stimulants |
Mechanism MECP2 stimulators(Methyl CpG binding protein 2 stimulators) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Rett Syndrome | Preclinical | United States | 01 Nov 2024 |