Last update 12 Apr 2025

Factor IX(Sangamo Therapeutics, Inc.)

Overview

Basic Info

Drug Type
Zinc-finger nucleases, AAV based gene therapy
Synonyms
Adlinacogene Civaparvovec, Factor IX gene therapy, SB FIX
+ [1]
Target
factor IX
Action-
Mechanism
Factor IX gene transference
Therapeutic Areas
Nervous System DiseasesCongenital DisordersEndocrinology and Metabolic Disease+ [2]
Active Indication
Mucopolysaccharidosis IMucopolysaccharidosis II
Inactive Indication
Hemophilia B
Originator Organization
Sangamo Therapeutics, Inc.Sangamo Therapeutics, Inc.
Active Organization
Sangamo Therapeutics, Inc.Sangamo Therapeutics, Inc.
Inactive Organization-
Drug Highest PhaseClinical
First Approval Date-
Regulation-
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Related

2
Clinical Trials associated with Factor IX(Sangamo Therapeutics, Inc.)
NCT04628871
/ Active, not recruitingNot Applicable
Long-Term Follow-up of Subjects Who Were Treated With SB-318, SB-913, or SB-FIX, for Targeted Genome Editing Into the Albumin Gene in the Liver
NCT02695160
/ TerminatedPhase 1
A Phase I, Open-Label, Ascending Dose Study to Assess the Safety and Tolerability of AAV2/6 Factor IX Gene Therapy Via Zinc Finger Nuclease (ZFN) Mediated Targeted Integration of SB-FIX in Adult Subjects With Severe Hemophilia B
100 Clinical Results associated with Factor IX(Sangamo Therapeutics, Inc.)
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100 Translational Medicine associated with Factor IX(Sangamo Therapeutics, Inc.)
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100 Patents (Medical) associated with Factor IX(Sangamo Therapeutics, Inc.)
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100 Deals associated with Factor IX(Sangamo Therapeutics, Inc.)
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R&D Status

10 top R&D records.
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IndicationHighest PhaseCountry/LocationOrganizationDate
Hemophilia BPhase 1
United States
Sangamo Therapeutics, Inc.Sangamo Therapeutics, Inc.
15 Nov 2016
Mucopolysaccharidosis IClinical
United States
Sangamo Therapeutics, Inc.Sangamo Therapeutics, Inc.
03 Nov 2020
Mucopolysaccharidosis IIClinical
United States
Sangamo Therapeutics, Inc.Sangamo Therapeutics, Inc.
03 Nov 2020
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Clinical Result

Indication
Phase
Evaluation
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Study
Phase
PopulationAnalyzed EnrollmentGroupResultsEvaluationPublication Date
NCT02695160 (CTgov)
Phase 1
Hemophilia B
1
spcvopvuzw = yyxnitecxo ivinmhjnlu (zpnzphqwrd, ubygrcjbwg - mtuhxqnxvk)
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-
19 Jul 2024
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Approval

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Regulation

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