Delving into the Latest Updates on HBG gene modified autologous CD34+ hematopoietic stem cells(Guangzhou Ruifeng) with Synapse

Overview

Drug Type

Gene therapy, Hematopoietic stem cell therapy

Synonyms

Target

Mechanism

HBG gene stimulators

Therapeutic Areas

Active Indication

Inactive Indication-

Originator Organization

Active Organization

Inactive Organization-

Drug Highest PhasePhase 1

First Approval Date-

Regulation-

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10 top R&D records.

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Indication	Highest Phase	Country/Location	Organization	Date
Transfusion-dependent Beta Thalassemia	Phase 1	CN	Guangzhou Ruifeng Biological Technology Co., Ltd.Startup	15 Dec 2022

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Indication

Phase

Evaluation

View All Results

Study	Phase	Population	Analyzed Enrollment	Group	Results	Evaluation	Publication Date


ASH2024	Not Applicable	Transfusion-dependent Thalassemia	-	RM-001	bkpvxhstak(mjuaopiptw) = No RM-001-related serious adverse event report. All of adverse events have been resolved. There were no deaths, discontinuations, or malignancies. xhvmciauau (jjjprvlfys )	-	09 Dec 2024
ChiCTR2100052858 \| ChiCTR2300069244 \| ChiCTR2100053406 (EHA2024) Manual	Phase 1	Beta-Thalassemia	16	RM-001	(inhzwyyrgj) = sonkkxnfzt ikvzuosnqk (ncxgqufodv ) Met View more	Positive	14 May 2024
ASH2023	Not Applicable	Transfusion-dependent Beta Thalassemia	7	RM-001	(mmflgyzakg) = ztsmtpyial yzpjylwgwf (ybcbnxjzzd ) View more	-	11 Dec 2023
EHA2022	Not Applicable	Transfusion-dependent Thalassemia	2	RM-001	(ysyqfjviub) = zkatiexcuo kjnszvrudb (rybmigodme )	Positive	12 May 2022