Delving into the Latest Updates on HBG gene modified autologous CD34+ hematopoietic stem cells(Guangzhou Ruifeng) with Synapse

Overview

Drug Type

Gene therapy, Hematopoietic stem cell therapy

Synonyms

Target

Mechanism

HBG gene stimulators

Therapeutic Areas

Active Indication

Inactive Indication-

Originator Organization

Active Organization

Inactive Organization-

Drug Highest PhasePhase 1

First Approval Date-

Regulation-

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10 top R&D records.

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Indication	Highest Phase	Country/Location	Organization	Date
Transfusion-dependent Beta Thalassemia	Phase 1	CN	Guangzhou Ruifeng Biological Technology Co., Ltd.Startup	15 Dec 2022

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Indication

Phase

Evaluation

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Study	Phase	Population	Analyzed Enrollment	Group	Results	Evaluation	Publication Date


ASH2024	Not Applicable	Transfusion-dependent Thalassemia	-	RM-001	eecxfgkuya(bzxdfemlzq) = No RM-001-related serious adverse event report. All of adverse events have been resolved. There were no deaths, discontinuations, or malignancies. hjadcqnxei (edmsxsrffg )	-	09 Dec 2024
ChiCTR2100052858 \| ChiCTR2300069244 \| ChiCTR2100053406 (EHA2024) Manual	Phase 1	Beta-Thalassemia	16	RM-001	(uvauowuxhg) = ipoixvqziz fcdlbmxptk (sosorktaxm ) Met View more	Positive	14 May 2024
ASH2023	Not Applicable	Transfusion-dependent Beta Thalassemia	7	RM-001	(mjcheoqfyx) = ayiauylcyj xeudvzgeaj (fgtqpobhdw ) View more	-	11 Dec 2023
EHA2022	Not Applicable	Transfusion-dependent Thalassemia	2	RM-001	(mzwrcrsgve) = iwcgugzwqi wrhsjqvgzd (mwmaqgvpty )	Positive	12 May 2022