Last update 01 Nov 2024
VGR-R01
Last update 01 Nov 2024
Overview
Basic Info
Drug Type AAV based gene therapy |
Synonyms A non-replicating recombinant adeno-associated virus vector serotype 8 delivering CYP4V2 gene, VGR R01, VGRR01 |
Target |
Mechanism CYP4V2 replacements(cytochrome P450 family 4 subfamily V member 2 replacements) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhasePhase 1 |
First Approval Date- |
RegulationOrphan Drug (US), Breakthrough Therapy (CN) |
Login to view timeline
Related
4
Clinical Trials associated with VGR-R01VGR-R01 治疗结晶样视网膜变性（BCD）的 I 期临床研究
[Translation] Phase I clinical study of VGR-R01 for the treatment of BCD
A Phase 1 Study to Assess the Safety and Tolerability of VGR-R01 in Patients With Bietti Crystalline Dystrophy
An Open-Label Safety Study of Single-dose VGR-R01 in Patients With Bietti Crystalline Dystrophy
100 Clinical Results associated with VGR-R01
Login to view more data
100 Translational Medicine associated with VGR-R01
Login to view more data
100 Patents (Medical) associated with VGR-R01
Login to view more data
100 Deals associated with VGR-R01
Login to view more data
R&D Status
10 top R&D records. to view more data
Login
| Indication | Highest Phase | Country/Location | Organization | Date |
|---|---|---|---|---|
| Bietti Crystalline Dystrophy | Phase 1 | CN | 01 Mar 2023 |
Login to view more data
Clinical Result
Clinical Result
Indication
Phase
Evaluation
View All Results
NEWS Manual  | Not Applicable | 12 | VGR-R01低剂量 | fhxcxopnvn(siyftvitwl) = yyqkdscoyc ohyhdelery (dhwghevolz ) | Positive | 10 May 2024 | |
VGR-R01中剂量 | fhxcxopnvn(siyftvitwl) = aqbjwiipdr ohyhdelery (dhwghevolz ) | ||||||
NCT05694598 (ASGCT2024) Manual | Phase 1/2 | Bietti Crystalline Dystrophy CYP4V2 biallelic mutation | 12 | VGR-R01 | jlzsipdkzn(aixwpuxxhc) = All patients experienced a treatment-emergent adverse event (TEAE) but just one eye inflammation was related to VGR-R01. zmtxxfwzws (vbswvecgaz ) | Positive | 07 May 2024 |
Login to view more data
Translational Medicine
Boost your research with our translational medicine data.
login
or
Deal
Boost your decision using our deal data.
login
or
Core Patent
Boost your research with our Core Patent data.
login
or
Clinical Trial
Identify the latest clinical trials across global registries.
login
or
Approval
Accelerate your research with the latest regulatory approval information.
login
or
Regulation
Understand key drug designations in just a few clicks with Synapse.
login
or
Chat with Hiro
Get started for free today!
Accelerate Strategic R&D decision making with Synapse, PatSnap’s AI-powered Connected Innovation Intelligence Platform Built for Life Sciences Professionals.
Start your data trial now!
Synapse data is also accessible to external entities via APIs or data packages. Empower better decisions with the latest in pharmaceutical intelligence.
Bio
Bio Sequences Search & Analysis
Sign up for free
Chemical
Chemical Structures Search & Analysis
Sign up for free