Drug Type AAV based gene therapy |
Synonyms Dual recombinant adeno-associated viral vectors encoding the human otoferlin gene, RRG 003, RRG003 |
Target |
Mechanism OTOF modulators(otoferlin modulators) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Inactive Organization- |
Drug Highest PhasePhase 1 |
First Approval Date- |
RegulationOrphan Drug (US) |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Deafness | Phase 1 | CN | 17 Nov 2022 | |
Deafness | Phase 1 | CN | 17 Nov 2022 | |
Hearing Loss | IND Approval | US | - |