Drug Type Gene therapy |
Synonyms- |
Target |
Action modulators |
Mechanism C9orf72 modulators(C9orf72-SMCR8 complex subunit modulators), Gene transference(Gene transference) |
Active Indication- |
Inactive Indication |
Originator Organization |
Active Organization- |
Inactive Organization |
License Organization- |
Drug Highest PhaseDiscontinuedPreclinical |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Amyotrophic Lateral Sclerosis | Preclinical | United States | - |