Drug Type ASO |
Synonyms ION 440 |
Target |
Mechanism MECP2 modulators(Methyl-CpG-binding protein 2 modulators) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhasePhase 1/2 |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Lubs X-Linked Mental Retardation Syndrome | Phase 2 | US | 21 Oct 2024 |