Drug Type AAV based gene therapy |
Synonyms Recombinant adeno-associated virus 8 (AAV8) expressing human retinoschisin (RS1) gene (Genevector) |
Target |
Mechanism XLRS1 stimulants(Retinoschisin stimulants) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhaseEarly Phase 1 |
First Approval Date- |
RegulationOrphan Drug (US) |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Retinoschisis | Phase 1 | CN | 17 Nov 2023 |