Drug Type RNA editing |
Synonyms AX 2404, AX2404 |
Target |
Action modulators |
Mechanism MECP2 modulators(Methyl-CpG-binding protein 2 modulators) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
License Organization- |
Drug Highest PhaseDiscovery |
First Approval Date- |
Regulation- |
| Indication | Highest Phase | Country/Location | Organization | Date |
|---|---|---|---|---|
| Rett Syndrome | Discovery | Netherlands | 01 Dec 2024 |





