Last update 15 Nov 2025

AAV-DMPK mRNA (Sanofi)

Overview

Basic Info

Drug Type
AAV based gene therapy
Synonyms
Adeno-associated virus vector serotype SAN011 encoding a microRNA against DMPK mRNA
Target
DMPK
Action
inhibitors
Mechanism
DMPK inhibitors(DM1 protein kinase inhibitors)
Therapeutic Areas
Nervous System DiseasesCongenital DisordersSkin and Musculoskeletal Diseases+ [1]
Active Indication
Myotonic Dystrophy
Inactive Indication-
Originator Organization
SanofiSanofi
Active Organization
SanofiSanofi
Inactive Organization-
License Organization-
Drug Highest PhasePreclinical
First Approval Date-
RegulationOrphan Drug (European Union)

Related

100 Clinical Results associated with AAV-DMPK mRNA (Sanofi)
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100 Translational Medicine associated with AAV-DMPK mRNA (Sanofi)
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100 Patents (Medical) associated with AAV-DMPK mRNA (Sanofi)
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100 Deals associated with AAV-DMPK mRNA (Sanofi)
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R&D Status

10 top R&D records.
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IndicationHighest PhaseCountry/LocationOrganizationDate
Myotonic DystrophyPreclinical
Switzerland
SanofiSanofi
11 Oct 2024
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Clinical Result

Indication
Phase
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Deal

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Core Patent

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Clinical Trial

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Approval

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Regulation

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