Last update 20 Mar 2025

Brogidirsen

Overview

Basic Info

Drug Type
ASO
Synonyms
+ [1]
Action
modulators, stimulants
Mechanism
DMD exon 44 modulators(Dystrophin exon 44 modulators), Dystrophin expression stimulants, RNA interference
Inactive Indication-
Originator Organization
Inactive Organization-
Drug Highest PhasePhase 2
First Approval Date-
RegulationRare Pediatric Disease (United States), Orphan Drug (European Union), Breakthrough Therapy (United States)
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Structure/Sequence

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R&D Status

10 top R&D records.
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IndicationHighest PhaseCountry/LocationOrganizationDate
Muscular Dystrophy, DuchennePhase 2
Japan
23 Jun 2021
Exon 44 Skipping Mutation Duchenne Muscular DystrophyPhase 2--
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Clinical Result

Indication
Phase
Evaluation
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Study
Phase
PopulationAnalyzed EnrollmentGroupResultsEvaluationPublication Date
Phase 1/2
Muscular Dystrophy, Duchenne
peptidyl arginine deiminase 2 (PADI2) | titin (TTN) | myomesin 2 (MYOM2)
6
nhfipmopuw(ubuxccmbbm) = jabeyvhwoa ybbqfdchey (tgdwcbddyu )
Positive
01 Jan 2025
nhfipmopuw(ubuxccmbbm) = voimxjwudy ybbqfdchey (tgdwcbddyu )
Phase 2
Muscular Dystrophy, Duchenne
dystrophin gene mutation amenable to exon 44 skipping
20
coevnoisct(sraehpivlb) = grgpzyibpk cojhrvlnmp (ivwjzukuyq )
Positive
03 Mar 2024
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Translational Medicine

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Deal

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Core Patent

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Clinical Trial

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Approval

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Regulation

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