12-month results from Part A of LIGHTHOUSE Trial reinforce ATSN-201's favorable safety pro durable structural and functional benefits in patients with X-linked retinoschisis Three-year data from Phase 1/2 trial confirm durable efficacy and tolerability of ATSN-101 in patients with Leber congenital amaurosis type 1 Atsena is advancing ATSN-201 and ATSN-101 into pivotal clinical trials in 2026 May 07, 2026 -- Atsena Therapeutics, a clinical-stage gene therapy company focused on using the life-cha

Fast Track Designation granted for RPTR-1-201, a T cell receptor bispecific, in triple-negative breast cancer Designation underscores the potential of RPTR-1-201 to address a serious disease with high unmet needs May 7, 2026 -- Repertoire® Immune Medicines, a biotechnology company pioneering the discovery and development of programmable T cell-targeted immune medicines, today announced that the U.S. Food and Drug Administration (FDA) has granted Fast Track Designation to RPTR-1-201 for the trea

May 06, 2026 -- InnoCare Pharma (HKEX: 9969; SSE: 688428), a leading biopharmaceutical company focusing on the treatment of cancer and autoimmune diseases, announced today that the Center for Drug Evaluation (CDE) of the China National Medical Products Administration (NMPA) has approved the Investigational New Drug (IND) application to initiate a clinical trial of its novel CDH17 targeted ADC, ICP-B208. CDH17 is a calcium-dependent cell adhesion protein that plays a key role in tumor cell proli

May 07, 2026 -- SK pharmteco today announced a strategic partnership with Axle Informatics and the National Institutes of Health (NIH) to advance the development of gene therapies for rare diseases. This partnership, focused on viral vector programs, underscores SK pharmteco’s commitment to the rare disease sector and its role as a key technical partner for leading research institutions. As a subcontractor to the NIH, SK pharmteco is working with Axle Informatics, the NIH’s primary contractor,

Catalyst Pharmaceuticals comes with a trio of approved drugs as Angelini Pharma expands its neuroscience offerings. Angelini Pharma is putting up $4.1 billion in a play for Catalyst Pharmaceuticals, scooping up three rare disease drugs that will allow the Italian company to enter the U.S. market. Angelini believes the buyout will establish the company as “a relevant global player in neurological rare diseases,” CEO Sergio Marullo di Condojanni said in a Thursday announcement. Created in 2002,

Enables more frequent FDA engagement, rolling Biologic License Application review, and the potential for Accelerated Approval and Priority Review upon successful clinical development Advances AP-SA02 on a faster path to potential approval and patient access May 7, 2026 -- Armata Pharmaceuticals, Inc. (NYSE American: ARMP) ("Armata" or the "Company"), a late clinical-stage biotechnology company focused on the development of high-purity, pathogen-specific bacteriophage therapeutics for the treatm

May 6, 2026 -- Diakonos Oncology Corp., a clinical-stage biotechnology company developing a new generation of immunotherapies to treat challenging and aggressive cancers, announced today that the U.S. Food and Drug Administration (FDA) has granted Fast Track designation to DOC1021, the Company's first-in-class, patient-derived double-loaded dendritic cell investigational therapy, for the treatment of unresectable or metastatic cutaneous melanoma. Unresectable or metastatic cutaneous melanoma re

May 6, 2026 -- Suzhou Ribo Life Science Co., Ltd. and Ribocure Pharmaceuticals AB ("Ribo", HKEX: 6938) today announced the achievement of a further milestone. This marks the third key milestone achieved in the research collaboration with Boehringer Ingelheim to discover novel therapies for liver disease, including metabolic dysfunction associated steatohepatitis (MASH). MASH is a serious and progressive form of fatty liver disease that can lead to fibrosis, cirrhosis, liver failure and liver ca

May 6, 2026 -- Alebund Pharmaceuticals (Jiangsu) Limited ("Alebund" or the "Company"), an integrated biopharmaceutical company focusing on developing innovative therapies for the treatment of renal diseases and related chronic conditions, today announced the completion of patient enrollment in the global Phase III pivotal multi-regional clinical trial (RESPOND-2, Study AP301-HP-03) of AP301, a novel fiber-iron-based phosphate binder, for the treatment of hyperphosphatemia. The trial was conducte

May 5, 2026 -- MingMed Biotechnology Co., Ltd, a biomedical firm focused on the discovery and development of novel therapeutics across multiple therapeutic areas, announced positive results from its Phase II clinical trial of QA102 in patients with intermediate dry age-related macular degeneration (AMD). Results of the study were presented in an oral presentation at the Association for Research in Vision and Ophthalmology (ARVO) 2026 annual meeting in Denver, Colorado. Intermediate dry AMD is a