[Translation] An open-label, multicenter, dose-escalation Phase I/II clinical study to evaluate the safety, tolerability and efficacy of FT-001 administered subretinal space in subjects with retinal degeneration associated with biallelic RPE65 variants
本研究是一项单臂、开放标签、多中心的I/II期临床研究,旨在评价FT-001对RPE65双等位基因变异相关的视网膜变性受试者的安全性、耐受性和有效性。
[Translation] This study is a single-arm, open-label, multicenter Phase I/II clinical study designed to evaluate the safety, tolerability and efficacy of FT-001 in subjects with retinal degeneration associated with RPE65 biallelic variants.