Drug Type AAV based gene therapy |
Synonyms Adenovirus Associated Viral Vector Serotype 8 Containing The Human Cngb3 Gene, Adenovirus associated viral vector serotype 8 containing the human CNGB3 gene - MeiraGTx, Entacingene Turiparvovec + [4] |
Target |
Mechanism CNGB3 gene stimulants(Cyclic nucleotide-gated cation channel beta-3 gene stimulants) |
Therapeutic Areas |
Active Indication |
Inactive Indication |
Originator Organization |
Active Organization |
Inactive Organization |
Drug Highest PhasePhase 2 |
First Approval Date- |
RegulationPRIME (EU), Orphan Drug (EU), Fast Track (US) |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Color Vision Defects | Phase 2 | US | 03 Jan 2023 | |
Achromatopsia 1 | Phase 2 | US | 16 Jan 2017 | |
Achromatopsia 1 | Phase 2 | GB | 16 Jan 2017 | |
Achromatopsia 1 | Phase 1 | GB | 16 Jan 2017 | |
Achromatopsia 1 | Phase 1 | US | 16 Jan 2017 | |
Achromatopsia 3 | Phase 1 | US | 16 Jan 2017 | |
Achromatopsia 3 | Phase 1 | GB | 16 Jan 2017 | |
Achromatopsia 3 | Phase 1 | US | 16 Jan 2017 | |
Achromatopsia 3 | Phase 1 | GB | 16 Jan 2017 |
Phase 1/2 | 23 | (Low Dose AAV - CNGB3) | nkxdzwzzzj(fcgaveuetn) = grntpgsyso yumlywbzhc (mqnybsxcgd, mrhlljuyhx - hqajmezaxy) View more | - | 08 Mar 2023 | ||
(Intermediate Dose AAV-CNGB3) | nkxdzwzzzj(fcgaveuetn) = peqinhbnxo yumlywbzhc (mqnybsxcgd, qmulnanmtb - jykmbqjazz) View more |