Last update 21 Nov 2024

TSHA-102

Overview

Basic Info

Drug Type
AAV based gene therapy
Synonyms
Target
Mechanism
MECP2 modulators(Methyl-CpG-binding protein 2 modulators), Gene transference
Active Indication
Inactive Indication-
Active Organization
Inactive Organization-
Drug Highest PhasePhase 1/2
First Approval Date-
RegulationRare Pediatric Disease (US), Orphan Drug (EU), Fast Track (US), Innovative Licensing and Access Pathway (GB), Regenerative Medicine Advanced Therapy (US)
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R&D Status

10 top R&D records.
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IndicationHighest PhaseCountry/LocationOrganizationDate
Rett SyndromePhase 2
CA
06 Mar 2023
Rett SyndromePhase 2
US
06 Mar 2023
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Clinical Result

Indication
Phase
Evaluation
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Study
Phase
PopulationAnalyzed EnrollmentGroupResultsEvaluationPublication Date
Phase 1/2
2
TSHA-102 Low Dose Cohort
(adult patients)
(colrwboksm) = None ktpzwbprzk (fopmqhpano )
Positive
18 Jun 2024
Phase 1/2
2
TSHA-102 low dose cohort
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Positive
18 Jun 2024
Phase 1/2
1
jxdqimnzqd(vpzxqfobgm) = No marked changes bbkzetkeeg (ygaqqqutqe )
Positive
14 Aug 2023
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Clinical Trial

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Approval

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Regulation

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