Drug Type Gene editing |
Synonyms ART001 |
Target |
Mechanism TTR modulators(Transthyretin modulators) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhasePhase 1 |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Transthyretin cardiac amyloidosis | Phase 1 | CN | 20 Oct 2023 |
ChiCTR2400081216 (NEWS) Manual | Not Applicable | 10 | mucwyjtfab(krvtiilcqe) = 给药后4周,高剂量组受试者外周TTR蛋白较基线即可平均下降90%以上。 vsjjexnfrg (qoscvgrxbx ) View more | Positive | 27 May 2024 |